ASPA gene
Showing 1 - 25 of 5,842
Canavan Disease Trial in Dayton (rAAV-Olig001-ASPA, Levetiracetam, Prednisone)
Enrolling by invitation
- Canavan Disease
- rAAV-Olig001-ASPA
- +2 more
-
Dayton, OhioDayton Children's Hospital
Jun 23, 2022
Canavan Disease Trial in Boston (AAV9 BBP-812)
Recruiting
- Canavan Disease
- AAV9 BBP-812
-
Boston, MassachusettsMassachusetts General Hospital (MGH); Center for Rare Neurologic
Mar 12, 2022
Liver Biopsy Following Gene Therapy For Hemophilia
Not yet recruiting
- Hemophilia A
- Hemophilia B
- Liver Biopsy
-
Memphis, TennesseeSt. Jude Children's Research Hospital
Jun 27, 2023
Leber Congenital Amaurosis Trial in Shanghai (HG004)
Recruiting
- Leber Congenital Amaurosis
- HG004
-
Shanghai, Shanghai, ChinaXinhua Hospital affiliated with Shanghai Jiao Tong UniversitySch
Oct 12, 2023
Study of Retinal Dystrophies Associated With Rare
Active, not recruiting
- Inherited Retinal Degeneration
- Retinitis Pigmentosa
-
Phoenix, Arizona
- +23 more
Jan 24, 2023
Leber Congenital Amaurosis Trial in Shanghai (HG004)
Recruiting
- Leber Congenital Amaurosis
- HG004
-
Shanghai, Shanghai, ChinaXinhua Hospital affiliated with Shanghai Jiao Tong University Sc
Sep 26, 2023
Heart Failure, Diastolic, Heart Failure With Preserved Ejection Fraction Trial in Durham, Dallas (AAV1/SERCA2a)
Recruiting
- Heart Failure, Diastolic
- Heart Failure With Preserved Ejection Fraction
- AAV1/SERCA2a
-
Durham, North Carolina
- +1 more
Sep 23, 2023
H19 in Acute Lymphoblastic Leukemia.
Not yet recruiting
- Acute Lymphoid Leukemia
- (no location specified)
Jul 11, 2023
Acute Myeloid Leukemia Trial in Taipei
Enrolling by invitation
- Acute Myeloid Leukemia
-
Taipei, TaiwanNational Taiwan University Hospital
Aug 9, 2023
Genomic Structural Variation in Cancer Susceptibility
Active, not recruiting
- Breast Cancer
- +5 more
-
New York, New YorkMemorial Sloan Kettering Cancer Center
Dec 23, 2022
Clinical Significance and Coexistence of Polymorphisms of
Active, not recruiting
- Ligament; Laxity
- Recurrent Patellar Dislocation
- genetic test
- Beighton joint laxity test
-
Lodz, Lodzkie Voivodeship, Poland
- +1 more
Feb 28, 2023
Breastmilk as a Source of Lactocytes
Recruiting
- Breastmilk Collection
- Micronutrients
- Collection of breastmilk
-
Stuttgart, GermanyUniversity of Hohenheim
May 12, 2023
Differentiate Between Systemic Inflammation and Infection After
Not yet recruiting
- Infections
- Sepsis
- blood leucocyte transcriptomics
- (no location specified)
Oct 30, 2023
Long Term Follow-Up for RGX-111
Enrolling by invitation
- Mucopolysaccharidosis I
- No Intervention
-
Orange, California
- +2 more
Oct 25, 2023
Iron, Alpha-Synuclein, and Lymphocyte-activation Gene-3 in
Not yet recruiting
- Brain Ischemia
- Serum Iron
- +7 more
-
Aswan, EgyptAswan University Hospital
Mar 7, 2023
Duchenne Muscular Dystrophy Trial in Worldwide (PF-06939926, Placebo)
Recruiting
- Duchenne Muscular Dystrophy
- PF-06939926
- Placebo
-
Little Rock, Arkansas
- +54 more
Jan 18, 2023
(SNPs) in Metalloproteinases Genes With Risk of Primary Knee
Recruiting
- Metalloproteinase SNPs -1575 G/A MMP-2, 836 A/G MMP-9 and -77 A/G MMP-13 and Risk for Developing Knee Osteoarthritis in Greek Population
- No intervention, Patients selection based on clinical symptoms and radiological imaging
-
Thessaloníki, Athens, Greece3rd Orthopedic Department , Pagageorgiou Hospital
Aug 17, 2022
Learn More About NTRK Gene Fusion Positive in Solid Tumor in
Not yet recruiting
- Advanced or Recurrent Solid Tumor Harboring an NTRK Gene Fusion
- No Drug
-
Multiple Locations, JapanMany Locations
Mar 20, 2023
Beta Thalassaemia Trial in Milan (Safety and Efficacy assessments)
Active, not recruiting
- Beta Thalassaemia
- Safety and Efficacy assessments
-
Milan, ItalyOspedale San Raffaele - Telethon Institute for Gene Therapy (OSR
Nov 22, 2022
l Gene Editing Therapy for Cardiovascular Disease
Not yet recruiting
- Atherosclerotic Cardiovascular Disease
- +2 more
-
Auckland, New Zealand
- +2 more
Oct 31, 2023
Prognosis of Blood Immune Cells After Cardiopulmonary Bypass
Recruiting
- Acute Kidney Injury
- Gene sequencing
-
Hangzhou, Zhejiang, ChinaThe Second Affiliated Hospital of Zhejiang University anesthesio
May 15, 2023
Cardiovascular Diseases, Cohort Studies, Genotype Trial in Vandœuvre-lès-Nancy (biological, genetic, other, behavioral,
Not yet recruiting
- Cardiovascular Diseases
- +4 more
- Blood and urine samples
- +20 more
-
Vandœuvre-lès-Nancy, Lorraine, FranceRossignol
Jun 14, 2023